Pelabresib DAK539 PHASE3
Drug Profile
ModalitySmall molecule
RouteOral
Therapy AreaOncology
Peak Sales Est$2000M
Formulations[]
Companies
NVS (ORIGINATOR)100%
Mechanism: BET inhibitor
Expert: Bromodomain and extra-terminal domain inhibitor, modulating gene transcription
Everyday: Blocks proteins that help cancer cells grow
Targets: ["BET"]
Programs (1)
IndicationStageKey StudyRegional Status
MF (JAK-naive)PHASE3MANIFEST-2[]
Upcoming Catalysts (2)
Pelabresib - Myelofibrosis - EU Filing/Approval 2026
Pelabresib - Myelofibrosis - Ph3 - Start (MANIFEST-3) 2026
Notes
BET inhibitor (BRD2/3/4) for myelofibrosis in combination with ruxolitinib. First-in-class BET inhibitor in this indication; targets transcriptional dysregulation driving disease pathophysiology.
Data from Supabase · Updated 2026-03-24