Myelofibrosis

MF · Oncology · 4 drugs · 4 indications

Myeloproliferative neoplasm with bone marrow fibrosis.
Competitive Landscape (4 drugs)
DrugCompanyMechanismModalityRouteStage
PelabresibNVSBET inhibitorSmall moleculeOralPHASE3
VonjoSOBIJAK2/IRAK1 inhibitorSmall moleculePOAPPROVED
JakafiJAK1/JAK2 inhibitorSmall moleculePOAPPROVED
OjjaaraJAK1/JAK2 inhibitorSmall moleculePOAPPROVED
Indications (4)
Myelofibrosis (intermediate/high risk)
Jakafi APPROVED
Myelofibrosis with anemia
Ojjaara APPROVED
Myelofibrosis with severe thrombocytopenia
Vonjo APPROVED
Myelofibrosis (JAK-inhibitor naive)
Pelabresib PHASE3
Upcoming Catalysts
Pelabresib - Myelofibrosis - EU Filing/ApprovalREGULATORY
NVS2026
Pelabresib - Myelofibrosis - Ph3 - Start (MANIFEST-3)CLINICAL
NVS2026
Vonjo - MF (severe thrombocytopenia) - Ph3 - Confirmatory (PACIFICA)CLINICAL
SOBI2026-2027
Data from Supabase · Updated 2026-03-24