Neuromyelitis optica spectrum disorder

NMOSD · Rare Disease · 3 drugs · 1 indications

Autoimmune CNS disorder affecting optic nerves and spinal cord.
Competitive Landscape (3 drugs)
DrugCompanyMechanismModalityRouteStage
EnspryngROG.SWAnti-IL-6R (Recycling)AntibodySCAPPROVED
UltomirisAZNC5 inhibitorAntibodyIVAPPROVED
UPLIZNAAMGNAnti-CD19 monoclonal antibodyMonoclonal antibodyIVAPPROVED
Indications (1)
Neuromyelitis Optica Spectrum Disorder
Enspryng APPROVEDUltomiris APPROVEDUPLIZNA APPROVED
Upcoming Catalysts
Ultomiris - IgAN - Ph3 - Topline (ICAN)CLINICAL
AZNH1 2026
Ultomiris - HSCT-TMA - Ph3 - ToplineCLINICAL
AZNH1 2026
Data from Supabase · Updated 2026-03-24