HemA · Rare Disease · 9 drugs · 6 indications
| Drug | Company | Mechanism | Modality | Route | Stage |
|---|---|---|---|---|---|
| Denecimig | NVO, GMAB | FVIIIa mimetic bispecific antibody | Bispecific antibody | SC | FILED |
| NXT007 | ROG.SW | FVIIIa mimetic bispecific antibody | Bispecific antibody | SC | PHASE2 |
| Hemlibra | ROG.SW | FVIIIa mimetic bispecific antibody | Bispecific | SC | APPROVED |
| Adynovate | — | Factor VIII replacement | Protein | IV | APPROVED |
| Alhemo | NVO | Anti-TFPI (tissue factor pathway inhibitor) antibody | Antibody | SC | APPROVED |
| Hympavzi | — | Anti-TFPI (tissue factor pathway inhibitor) antibody | Antibody | SC | APPROVED |
| Fitusiran | — | Anti-antithrombin siRNA (RNAi) | siRNA | SC | APPROVED |
| Altuviiio | SOBI | Extended half-life recombinant Factor VIII | Recombinant protein | IV | APPROVED |
| Elocta | SOBI | — | Recombinant protein | IV | APPROVED |