Atypical hemolytic uremic syndrome

aHUS · Rare Disease · 2 drugs · 1 indications

Complement-mediated thrombotic microangiopathy.
Competitive Landscape (2 drugs)
DrugCompanyMechanismModalityRouteStage
SolirisAZNC5 inhibitorAntibodyIVAPPROVED
UltomirisAZNC5 inhibitorAntibodyIVAPPROVED
Indications (1)
Atypical hemolytic uremic syndrome
Soliris APPROVEDUltomiris APPROVED
Upcoming Catalysts
Ultomiris - IgAN - Ph3 - Topline (ICAN)CLINICAL
AZNH1 2026
Ultomiris - HSCT-TMA - Ph3 - ToplineCLINICAL
AZNH1 2026
Data from Supabase · Updated 2026-03-24