CHAPLE disease

CHAPLE · Rare Disease · 1 drugs · 1 indications

CD55 deficiency with hyperactivation of complement.
Competitive Landscape (1 drugs)
DrugCompanyMechanismModalityRouteStage
VeopozREGNC5 inhibitorMonoclonal antibodySCAPPROVED
Indications (1)
CHAPLE disease (CD55-deficient PLE)
Veopoz APPROVED
Upcoming Catalysts
Pozelimab+Cemdisiran - gMG - Ph3 Topline (NIMBLE)CLINICAL
REGN2026-2027
Data from Supabase · Updated 2026-03-24