Amyotrophic lateral sclerosis

ALS · Neurology · 1 drugs · 1 indications

Progressive motor neuron disease.
Competitive Landscape (1 drugs)
DrugCompanyMechanismModalityRouteStage
Ulefnersen4578Antisense Oligonucleotide (FUS)Antisense oligonucleotideINTRATHECALPHASE3
Indications (1)
FUS-mutation ALS
Ulefnersen PHASE3
Upcoming Catalysts
Ulefnersen - FUS-ALS - Ph3 - Topline (FUSION)CLINICAL
4578H2 2026
Data from Supabase · Updated 2026-03-24