Homozygous familial hypercholesterolemia
HoFH · CVRM · 1 drugs · 1 indications
Ultra-rare genetic disorder with severely elevated LDL-C from birth.
Competitive Landscape (1 drugs)
| Drug | Company | Mechanism | Modality | Route | Stage |
|---|
| EVKEEZA | REGN | ANGPTL3 inhibitor (monoclonal antibody) | Monoclonal antibody | IV | APPROVED |
Indications (1)
Homozygous familial hypercholesterolemia
Data from Supabase · Updated 2026-03-24